3rd Annual

Orphan Drug Summit 2026

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Meet Our Featured Speakers

Alan Minsk

Alan Minsk

Arnall Golden Gregory LLP

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Vishal Singal

Vishal Singal

Beghou Consulting

Alan Minsk

Alan Minsk

Arnall Golden Gregory LLP

Arjun Channi

Arjun Channi

Sanofi

THE PREMIER FORUM FOR ORPHAN DRUG THERAPIES AND RARE DISEASES

Welcome to the Orphan Drug Summit 2026, where leading industry experts and innovators come together to explore the latest technologies and manufacturing know-how shaping the future of the rare disease healthcare industry.

The healthcare industry is transforming therapies for rare diseases, focusing on improved delivery, stability, and bioavailability. Manufacturers must navigate complex regulations to develop drugs that meet rigorous safety standards, providing solutions that are safe and effective.

Join us to explore breakthroughs in orphan drug development, share collective knowledge, and advance progress in treating rare diseases.

key topics for

Current market trends and future projections for orphan drugs

Explore the driving forces behind orphan drug market growth, with a focus on the breakthrough potential of rare disease therapies.

Novel strategies for formulating and delivering orphan drug therapies

Explore cutting-edge innovations in drug delivery systems that are revolutionizing rare disease therapies and setting new standards in patient care.

Recent case studies and real-world evidence in patient advocacy

Gain insights from real-world evidence and patient advocacy case studies to enhance decision-making and advance therapies for rare diseases.

Tech-driven innovation and advances in rare disease therapy development

Learn how technology-driven innovations are transforming the development and commercialization of rare disease therapies and enhancing accessibility.

Health equity and patient perspectives in orphan drug management

Integrate patient feedback into the development of orphan drugs to ensure inclusive access to innovative treatments and promote treatment equity.

Regulatory and policy shifts in the ecosystem of rare disease therapeutics

Learn about the evolving regulatory landscape for rare disease therapeutics and its impact on innovation and patient access.

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INDUSTRY TOPICS

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NETWORKING EVENTS

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LEADING EXPERTS

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Q&A SESSIONS

Latest News

  • MARKET TRENDS

    14 Dec 2025

    Rare Disease Boom Redefines Pharma Strategy
  • INNOVATION

    11 Dec 2025

    An Experimental Gene Therapy Signals New Hope for Rare Disorders
  • INVESTMENT

    9 Dec 2025

    High Risk, High Impact: Rare Disease Biotech Reclaims Investor Attention
  • TECHNOLOGY

    8 Dec 2025

    AI Models Take on Medicine’s Rarest Challenges

BioCryst Bets on Convenience in High-Stakes HAE Deal

BioCryst Bets on Convenience in High-Stakes HAE Deal

PARTNERSHIPS

4 Dec 2025

Pending Astria acquisition centres on long-acting therapy as drugmakers seek more convenient treatments for rare diseases

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Expert Speakers

Vanessa Navarro

Danaher Corporation

Namrita Negi

Deloitte

Arjun Channi

Sanofi

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Past Attendees

Danaher Corporation

Deloitte

Global Genes

Sanofi

Becton Dickinson

Tessera Therapeutics

Charles River

Körber

Chiesi USA, Inc.

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