Meet Our Featured Speakers
THE PREMIER FORUM FOR ORPHAN DRUG THERAPIES AND RARE DISEASES
Welcome to the Orphan Drug Summit 2026, where leading industry experts and innovators come together to explore the latest technologies and manufacturing know-how shaping the future of the rare disease healthcare industry.
The healthcare industry is transforming therapies for rare diseases, focusing on improved delivery, stability, and bioavailability. Manufacturers must navigate complex regulations to develop drugs that meet rigorous safety standards, providing solutions that are safe and effective.
Join us to explore breakthroughs in orphan drug development, share collective knowledge, and advance progress in treating rare diseases.
key topics for
Current market trends and future projections for orphan drugs
Explore the driving forces behind orphan drug market growth, with a focus on the breakthrough potential of rare disease therapies.
Novel strategies for formulating and delivering orphan drug therapies
Explore cutting-edge innovations in drug delivery systems that are revolutionizing rare disease therapies and setting new standards in patient care.
Recent case studies and real-world evidence in patient advocacy
Gain insights from real-world evidence and patient advocacy case studies to enhance decision-making and advance therapies for rare diseases.
Tech-driven innovation and advances in rare disease therapy development
Learn how technology-driven innovations are transforming the development and commercialization of rare disease therapies and enhancing accessibility.
Health equity and patient perspectives in orphan drug management
Integrate patient feedback into the development of orphan drugs to ensure inclusive access to innovative treatments and promote treatment equity.
Regulatory and policy shifts in the ecosystem of rare disease therapeutics
Learn about the evolving regulatory landscape for rare disease therapeutics and its impact on innovation and patient access.
INDUSTRY TOPICS
NETWORKING EVENTS
LEADING EXPERTS
Q&A SESSIONS
Latest News
MARKET TRENDS
14 Dec 2025
Rare Disease Boom Redefines Pharma StrategyINNOVATION
11 Dec 2025
An Experimental Gene Therapy Signals New Hope for Rare DisordersINVESTMENT
9 Dec 2025
High Risk, High Impact: Rare Disease Biotech Reclaims Investor AttentionTECHNOLOGY
8 Dec 2025
AI Models Take on Medicine’s Rarest Challenges
BioCryst Bets on Convenience in High-Stakes HAE Deal

PARTNERSHIPS
4 Dec 2025
Pending Astria acquisition centres on long-acting therapy as drugmakers seek more convenient treatments for rare diseases
they've attended our events
Expert Speakers
Vanessa Navarro
Danaher Corporation
Namrita Negi
Deloitte
Arjun Channi
Sanofi
Past Attendees
Danaher Corporation
Deloitte
Global Genes
Sanofi
Becton Dickinson
Tessera Therapeutics
Charles River
Körber
Chiesi USA, Inc.













